Efficient inhibition of the Alzheimer's disease β-secretase by membrane targeting

Research output: Contribution to journalResearch articleContributedpeer-review

Contributors

  • Lawrence Rajendran - (Author)
  • Anja Schneider - (Author)
  • Georg Schlechtingen - , TUD Dresden University of Technology (Author)
  • Sebastian Weidlich - , TUD Dresden University of Technology (Author)
  • Jonas Ries - , TUD Dresden University of Technology (Author)
  • Tobias Braxmeier - , TUD Dresden University of Technology (Author)
  • Petra Schwille - , TUD Dresden University of Technology (Author)
  • Jörg B. Schulz - , University Medical Center Göttingen (Author)
  • Cornelia Schroeder - , TUD Dresden University of Technology (Author)
  • Mikael Simons - (Author)
  • Gary Jennings - (Author)
  • Hans Joachim Knölker - , Chair of Organic Chemistry II (Author)
  • Kai Simons - (Author)

Abstract

β-Secretase plays a critical role in β-amyloid formation and thus provides a therapeutic target for Alzheimer's disease. Inhibitor design has usually focused on active-site binding, neglecting the subcellular localization of active enzyme. We have addressed this issue by synthesizing a membrane-anchored version of a β-secretase transition-state inhibitor by linking it to a sterol moiety. Thus, we targeted the inhibitor to active β-secretase found in endosomes and also reduced the dimensionality of the inhibitor, increasing its local membrane concentration. This inhibitor reduced enzyme activity much more efficiently than did the free inhibitor in cultured cells and in vivo. In addition to effectively targeting β-secretase, this strategy could also be used in designing potent drugs against other membrane protein targets.

Details

Original languageEnglish
Pages (from-to)520-523
Number of pages4
JournalScience
Volume320
Issue number5875
Publication statusPublished - 25 Apr 2008
Peer-reviewedYes

External IDs

PubMed 18436784

Keywords

ASJC Scopus subject areas