Wie Designer-Rekombinasen Erbkrankheiten heilen könnten
Publikation: Beitrag in Fachzeitschrift › Forschungsartikel › Eingeladen
Beitragende
Abstract
Recent advances in nuclease-based genome editing allow for the correction of many point-mutations causing diseases. However, correcting genetic alterations caused by larger chromosomal rearrangements remain challenging with this approach. Designer-recombinases promise to fill this gap as demonstrated by the development of a heterodimeric Cre-based site-specific recombinase system. This system can functionally correct a large gene inversion frequently found in patients with severe Hemophilia A.
Details
Originalsprache | Deutsch |
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Fachzeitschrift | Biospektrum |
Jahrgang | 27 |
Publikationsstatus | Veröffentlicht - März 2021 |
Peer-Review-Status | Nein |
Externe IDs
Scopus | 85103171326 |
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